Project aims and fields of work

Through eight complimentary project work packages, TIRCON aims to achieve:

1. the setup of an international NBIA registry
2. the implementation of a biobank
3. the development of biomarkers for the disease
4. the conduction of a randomized clinical trial of the iron-chelating
    drug Deferiprone in PKAN
5. the preclinical development of new compounds for the
    treatment of PKAN

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